THE LARGE PRICE TAG FOR A BRAND-NEW MUSCLE DYSTROPHY DRUG IS CREATING ANGER. THEY ARE DELAYING THE LAUNCH AFTER PUBLIC OUTRAGE AND WASHINGTON LEGISLATORS OBTAINED ENTAILED. CBS 2'' S DR. MAX GOMEZ WITH THE CONTROVERSY. THAT'' S RIGHT, PEOPLE. THE DEFLAZACORT IS NOT A TREATMENT BUT IT DOES SLOW THE PROGRESSION OF MUSCLE DYSTROPHY. IT'' S BEEN AVAILABLE IN EUROPE AND ASIA FOR SEVERAL YEARS BUT NOT IN THE U.S. AFTER THAT THE FDA PROVIDED IT ORPHAN MEDICINE CONDITIONS AND AFTERWARDS AMERICAN BUSINESS GOT APPROVAL LAST WEEK BUT WHAT MUST HAVE BEEN GOOD NEWS QUICKLY GOT ANGRY.DYLAN NELSON
HAS A RARE FORM OF MUSCULAR DYSTROPHY CALLED DUCHENNE FOUND ALMOST SOLELY IN KIDS. THE LETHAL CONGENITAL DISEASE DETERIORATES HIS MUSCLES WITH TIME BUT ALSO FOR THE PAST ONE DECADE, THE STEROID DEFLAZACORT HAS ASSISTED. THIS IS A MEDICATION THAT INCLUDES LIKELY 3 YEARS OF WALKING FOR BOYS. SO PROBABLY DYLAN ENTERED INTO A WHEELCHAIR LATER 3 YEARS THAN HE WOULD HAVE. Reporter: SCIENTISTS AT UCLA RESEARCHING DUCHENNE. UP UNTIL CURRENTLY PEOPLE NEEDED TO DISCOVER A WAY TO OBTAIN THE MEDICINE FROM OVERSEAS. THE FDA-APPROVED THE DRUG UP FOR SALE IN THIS NATION LAST WEEK AND ALSO MARATHON PHARMACEUTICALS WAS ABOUT TO BEGINNING MARKETING IT UNTIL THE FIRM STATED IT WOULD FEE $89,000 A YEAR FOR DEFLAZACORT COMPARED TO JUST $1,200 FOR THE COMMON VARIATION ABROAD. THE PRICE HAS ANNOYED LAWMAKERS ON CAPITOL HILLSIDE WHO WILL CERTAINLY TAX MARATHON. MEDICATION FIRMS TIN COST United States ANY PRICE THEM. THAT'' S WHY WE HAVE THE GREATEST GLOBALLY RATES FOR MEDICATION. Reporter: THE FEDERAL GOVERNMENT HAS NO OVERSIGHT IN PRICES BUT BERNIE SANDERS IS CALLS FOR AN EXAMINATION. WE ARE GOING TO BE THEIR WORST HEADACHE. Press reporter: WE WANT TO COME TO A VERDICT THAT BRINGS THE BENEFIT OF THIS MEDICINE TO ALL PEOPLE WHO NEED IT DESPITE THEIR CAPABILITY TO PAY AND ALLOWS TO US CONTINUE FURTHER RESEARCH, THEY SAID.MARATHON DID NOT SAY
EXACTLY WHY IT HAD DELAYED LAUNCH OF THE MEDICATION BUT CLAIMED THAT CO-PAYS FOR INDIVIDUALS WOULD BE NO OR VERY LOW. OBVIOUSLY THAT SUGGESTS INSURER WOULD BE GROUND THE BILL FOR THE MEDICATION, AS WELL AS THOSE PRICES WOULD BE BORNE BY ALL OF United States.
